The Bone Marrow Transplant Experience


The following excerpt is taken from Chapter 20 of Childhood Leukemia: A Guide for Families, Friends, and Caregivers, 2nd Edition by Nancy Keene, copyright 1999 by O'Reilly & Associates, Inc. For book orders/information, call (800) 998-9938. Permission is granted to print and distribute this excerpt for noncommercial use as long as the above source is included. The information in this article is meant to educate and should not be used as an alternative for professional medical care.


Donating the marrow

Marrow is withdrawn (harvested) from the large bones of the hips. While the donor or patient (for autologous transplant) is under general anesthesia, the doctor inserts a large needle into the bones of the hips and withdraws bone marrow. This procedure is done up to fifty times to draw out a total of one to two pints. The entire process takes less than one hour. After marrow donation, some hospitals keep the donor overnight, while others discharge the same day if the donor is not in pain.

Because the amount of marrow that is removed contains less than five percent of the donor's developing blood cells, it only takes a few days for the body to replace the marrow. The donor or child is usually sore for a day or two, and may feel a bit tired for several days. The recovery time varies from donor to donor.

After no match was found for Christie in the 4,000 donors that we signed up and typed, I became her donor. We were just a partial match. Being her donor was just wonderful. It was Mother's Day weekend, and I was just full of faith and love. I thought this is it, God has given me a second chance to give life to this child. I had a very powerful feeling that it was so special that I could do this for my daughter. I really felt that this was it, it was going to work.

It was uncomfortable for a couple of days, and I was a little bruised. But the people there were wonderful, and they really followed me closely. I'm still on the registry; if someone called me tomorrow, I'd be on a plane. It's a very rewarding feeling, a gift from God.

•  •  •  •   •  

Jody's two-year-old brother Christoph was a perfect match. I stayed with him when he donated marrow, and my husband stayed with Jody. Christoph seemed to handle the marrow donation easily. Although he had some nausea in the recovery room, he was up and running around late that afternoon saying, "I the donor." He felt very proud. I knew he was somewhat sore because he said, "My diaper hurts."

The transplant

Prior to the actual transplant, the patient's bone marrow is destroyed using high-dose chemotherapy with or without radiation. This portion of treatment is called conditioning. The purpose of the high-doses of chemotherapy and radiation is to kill all remaining cancer cells in the body and make room in the bones for the new bone marrow or stem cells.

Conditioning regimens vary according to institution and protocol, and also depend on the medical condition and history of the patient. Typically, the chemotherapy is given for two to six days, and radiation (if part of conditioning) is given in multiple small doses over several days.

They got JaNette into her second remission in December, then gave her maintenance drugs to keep her there until they were ready to start transplant conditioning in April. So, unlike some of the other kids, she went to transplant healthy and strong. JaNette had 1200 rads of total body radiation in five increments--two the first day, two the second day, and one the third day. Then she had two days of incredibly strong chemotherapy, one day of rest, then the transplant.

The transplant itself consists of simply infusing the marrow or stem cells through a central venous catheter or IV into the patient, just like a blood transfusion. The marrow or stem cells travel through the blood vessels, eventually filling the empty spaces in the long bones. Engraftment is when the new marrow begins to produce healthy white cells, red cells, and platelets. This typically occurs from two to six weeks after transplantation. Complete recovery of all components of immune function can take from one to two years.

I couldn't believe how beautiful the bone marrow was--a bag of shimmering red liquid. It just glistened. It meant life.

•  •  •   •  •  

My dad donated marrow for my transplant. He said he was sore and doing the "bone marrow hop," but he made it to my room that day to see his marrow transfused into me. I really felt different as I was getting the bone marrow, like I was getting so much more energy.

•  •  •   •  •  

I cannot say enough good things about the transplant center. They were very family-oriented, allowed us in the room 24 hours a day. I was allowed to sleep in bed with her ( I just told the nurses to make sure to poke her and not me). The nurses were wonderful, and I still think of them as family. We didn't get very close to the other families; we tended to stay in our own child's room. One day a family would be there, then the next day they would be gone. I got to the point where I just didn't want to know.

•  •  •   •  •  

The transplant went well except that he was 50 days in the laminar flow room so that we couldn't touch him. Five years old and we couldn't touch him. We had these gloves that we could use to reach in. But Jody was such an accepting kid, he adjusted. We played a lot of cards and at night we'd turn off the lights, and he'd imagine soaring out the tenth floor window. He'd just fly out of that room. He was on hyperal (IV nutrition) and lots of prednisone and other drugs, and he had a few tantrums. Once he pulled out all of his needles and threw them against the wall. I thought that it was a pretty healthy response, but the social worker showed up immediately.

•  •  •   •  •  

We were prepared to stay five months in or near the transplant center, but we went home after only two and a half. She had the normal nausea, so she was on TPN (total parenteral nutrition) from transplant May 5 until the end of June. Until she could take her medications by mouth, I did some IVs at home. She had her last platelet transfusion in July. It took until the following June for her counts to normalize, and for her to start producing T cells. We feel lucky that things went so well.

Donor and patient confidentiality are closely guarded. The NMDP allows letter exchanges or meetings if both donor and recipient express a strong desire to do so, but only after a year has passed since the transplant.

Emotional responses

Bone marrow transplant takes a heavy emotional toll on the child, the parents, and the siblings. It can be a physically and mentally grueling procedure, with the possibility of months or years of aftereffects. Most transplant team members are extensively trained to meet the needs of the patient and family during the transplant and long convalescence. The team includes physicians and nurses, as well as psychiatrists, social workers, chaplains, educators, nutritionists, and child life therapists.

Christie had many painful complications after the unmatched allogeneic transplant. I remember lying next to her and saying, "Christie, if Mommy could take this away from you I would." She looked at me and said, "Mommy, I love you so much, I would never want you to go through this." But then she went on to say, "It's not so bad, I met a lot of people, we got to travel, Daddy didn't have to work, Danielle and Nicole got to spend time with Daddy." She just saw something positive in everything, even this terrible disease.

Christie was also very, very funny. She loved having me be the donor, and she started calling me her "blood sister." She kept saying, "Ma, when am I going to start being funny like you?" and I'd tell her that she was way beyond me. Her humor was contagious.

•  •  •   •  •  

Leah was feeling good and was very healthy when she went into the laminar air flow room. We lived near the transplant center, and she had at least twenty visitors a day. I think the visits and the nonstop telephone conversations really kept her spirits up. I think the hardest part of the transplant was being in the laminar air flow room (LAF). They gave me a sterilization wash, put me in some boots, and told me I couldn't touch anything. I felt like a space person. Then I went into the room for two months. I really missed touching people. I cried when I got out and hugged my mom.

•  •  •   •  •  

What helped me the most was the decorations and having a positive attitude. My mom decorated the area outside the LAF room with balloons, cards, and posters. It was hard to take the medicine, so my mom made a huge poster to mark off how well I did. Every time I took my medicine, I got a sticker. When I got one hundred stickers, I got some roller blades.

•  •  •   •  •  

I felt great during the transplant and at the center, but when we came home it was very, very difficult. We had just moved before my daughter was transplanted, so we didn't have a good support system in place. She had been in the hospital, then transplant center for almost a year, and then we had to stay at home for another year. For a few months she would spike a fever every time someone who was not in the family came in the house. So my young son could never go to friends to play or have friends over. We just stayed home. It was very hard, and we all felt very isolated.

Often so much time and energy is focused on the child who needs the transplant that the needs of the sibling donor are overlooked. Siblings need careful preparation for what is about to occur, and all questions need to be answered and concerns addressed. Parents need to be careful that the sibling donor realizes that the results of the BMT are out of everyone's control, and that the sibling is not responsible for either her brother's life or death.

Complications

Some children have a smooth journey through the transplant process, while others bounce from one life-threatening complication to another. Some children live, and some children die. There is no way to predict which children or teens will develop problems, nor is there any way to anticipate whether the new development will be merely an inconvenience or a catastrophe. This section will present some of the major complications that can develop post-transplant, and the experiences of several families in facing these problems.

Failure to engraft

Engraftment is when the donated marrow takes up residence in the patient's bones and begins to produce healthy blood cells. In cases where a child has received HLA-matched marrow from a sibling, engraftment failure is less than 5 percent. In contrast, children receiving marrow from partially HLA matched family members or unrelated donors, graft rejection occurs in 5 to 25 percent of patients.

Infections

Most infections following transplant come from organisms within the body (e.g., CMV, gut bacteria). Good handwashing and adequately controlled ventilation can help minimize infections with staph and fungi.

The immune system of healthy children quickly destroys any foreign invaders; not so with children who have undergone a bone marrow transplant. The diseased immune system of these children has been destroyed by chemotherapy and radiation to allow the healthy marrow or stem cells to grow. Until the new marrow or stem cells engraft and begin to produce large numbers of white cells (two to six weeks), children post-transplant are in danger of developing serious infections.

To prevent and combat bacterial infections, children receive large doses of several kinds of antibiotics if their temperature goes above 101°F (38.5°C) any time in the first weeks after transplant. Ironically, the antibiotics used to treat bacteria allow fungi to flourish. Fungal infections often follow prolonged neutropenia and antibiotics and can't be prevented easily.

Leah had so many problems with infections and getting her counts back up that she spent two years on steroids, cyclosporin, and monthly gammaglobulin.

•  •  •   •  •  

During the related mismatched allogeneic transplant, I developed no mouth sores, no infections, no GVHD. Just a headache the whole time. I do miss being an athlete, I do miss the friends that I lost, and I do miss my blond hair (it came back in brown, so I tried to dye it blond and it turned bright, fluorescent red). But I can deal with those things. To survive I think you need luck, a positive attitude, and a decorated room to help you stay cheery.

After the first month post-transplant, children are also susceptible to serious viral infections, most commonly herpes simplex virus, cytomegalovirus, and varicella zoster virus, particularly if they have GVHD. These can occur up to two years after the transplant. Viral infections are notoriously hard to treat, so many centers use prophylactic acyclovir or granciclovir or immunoglobulin to prevent these infections.

CMV is usually preventable if the patient and donor are both CMV-negative and all transfused blood products are CMV-negative or filtered to remove white blood cells.

Interstitial pneumonitis, a sometimes fatal form of pneumonia, is most common the second or third month post-transplant. It is very uncommon after autologous transplants and is most often associated with GVHD after allogeneic transplants.

Preventing infections is the best policy for those children who have had a bone marrow or stem cell transplant. The following are suggestions to minimize exposure to bacteria, viruses, and fungi:

For more information on infections, obtain the September 1993 BMT Newsletter, "Infections," or read Bone Marrow Transplants: A Book of Basics for Patients, by Susan Stewart.

Graft-versus-host disease (GVHD)

Graft-versus-host disease is a frequent complication of allogeneic bone marrow transplants. It does not occur with autologous or syngeneic transplants. In GVHD, the bone marrow or stem cells provided by the donor (graft) attack the tissues and organs of the BMT child (host). Approximately 30 to 50 percent of persons who have a related HLA-matched transplant develop some degree of GVHD. The incidence and severity of GVHD are increased for those children who receive unrelated or mismatched marrow, but are decreased if cells that cause GVHD are reduced prior to infusion. The majority of GVHD cases are mild, although some can be life-threatening.

There are two types of GVHD: acute GVHD and chronic GVHD. Patients can develop one type, both types, or neither. Acute GVHD usually occurs at the time of engraftment or shortly thereafter. Donor cells identify the patient's cells as foreign, and may attack the patient's skin, liver, stomach, or intestines. Allogeneic BMT patients are given drugs before and after transplant in an attempt to prevent GVHD. Symptoms of acute GVHD can range from mild skin rash to severe, sometimes fatal infections, or liver, stomach, and intestinal problems. Acute GVHD is treated with cyclosporin and steroids (prednisone, dexamethasone). Methotrexate may be given to prevent GVHD.

JaNette's transplant was on May 5 and her ANC was up to 1000 on May 30. That's when her graft-versus-host started. It doesn't look like a regular rash, more like pinpoint red dots under the skin. It's very itchy, and then it starts to peel. She looked like she had leprosy! She had very little internal graft-versus-host disease. She's a year and a half post-transplant, and she still broke out in a rash the last time they tried to taper her off the cyclosporin.

•  •  •   •  •  

Ryan died from acute graft-versus-host disease. It destroyed his liver. It was a hard death, and we felt that it robbed us of whatever time he would have had left if he didn't have the BMT.

Chronic GVHD usually develops after the third month post-transplant. It primarily affects the skin (itchy rash, discoloration of the skin, tightening of the skin, hair loss), eyes (dry, light-sensitive), mouth and esophagus (dry, tooth decay, difficulty swallowing), intestines (diarrhea, cramping, weight loss), liver (jaundice), lungs (shortness of breath, wheezing, coughing ), and joints (decreased mobility). This list may seem overwhelming, but remember that only some patients develop chronic GVHD, and those who do may experience all, a few, or only one of these symptoms.

A year and a half after the transplant, they tried to taper my daughter off the cyclosporin. Her liver function counts went way up, and she broke out in a rash all over her body. The bottoms of her feet were so blistered that she couldn't walk. She has permanent dark splotches all over her torso, but the ones on her face and neck gradually faded away.

•  •  •   •  •  

I wasn't supposed to go out in the sun after my transplant, but I did anyway. The sun aggravated the mild GVHD that I had and I turned blotchy. I had itchy light and dark patches on my stomach and face. I had to go back on steroids.

Veno-occlusive disease

Veno-occlusive disease (VOD) is a complication that can occur after bone marrow or stem cell transplantation in which the flow of blood through the liver becomes obstructed. Children who have had more than one transplant or previous liver problems are more at risk to develop VOD. It can occur gradually or very quickly. Symptoms of VOD include jaundice (yellowing of the skin), an enlarged liver, pain in the upper right abdomen, fluid in the abdomen, and unexplained weight gain. Treatment includes fluid restriction, diuretics (such as furosemide), anti-clotting medications, and removal of all but the most essential amino acids from IV nutrition (hyperalimentation).